Some children in Northern Ireland who live with a severe form of muscular dystrophy will be able to access new medication on the health service, BBC News understands. The move from the Belfast Health ...

Givinostat is an oral histone deacetylase (HDAC) inhibitor approved by the FDA in 2024 to treat Duchenne patients ages 6 ...

His parents Stephen and Jenny have asked Sheffield Children's NHS Foundation Trust to approve the use of drug givinostat, ...

WASHINGTON, June 12, 2025 /PRNewswire/ -- Parent Project Muscular Dystrophy (PPMD), a nonprofit organization leading the fight to end Duchenne muscular dystrophy (Duchenne), is pleased to announce the ...

Please provide your email address to receive an email when new articles are posted on . The FDA has approved an abbreviated new drug application for a generic version ...

Duchenne muscular dystrophy (DMD) results from changes in the DMD gene. Children may inherit DMD gene changes from their parents or have spontaneous gene changes. The DMD gene tells the body how to ...

The University at Albany and Virginia Commonwealth University were awarded a $6.5 million NIH grant to establish a federal ...

Duchenne muscular dystrophy (DMD) is an inherited muscle disorder that causes progressive breakdown of muscle tissue. Symptoms typically begin in early childhood, and most parents and caregivers ...

Each week, this series shares MarionMade! stories of our many wonderful people, places, products and programs in the greater Marion community. To read more positive stories of Marion, or to share some ...

Iowa City Robotics, a team of robot-building high schoolers, gave a 16-month-old boy the chance to explore the world on wheels. Modified with a push-to-accelerate button, extra Styrofoam padding, and ...

An 11-year-old girl with muscular dystrophy was given a cheer as she walked down the hallway of Southampton Hospital as part ...

Charlotte and Tom Hardwick, both 33 and from Beechdale in Nottingham, have different types of muscular dystrophy and need ...